NanoCas, an ultracompact nuclease, enables efficient muscle editing in NHPs using a single AAV - advancing gene editing for hard-to-target tissues.
A research group at Umeå University has developed new advanced light-controlled tools that enable precise control of proteins in real time in living cells.
January 31, 2025 expert reaction to NICE final draft guidance on exagamglogene autotemcel (exa-cel) for severe sickle cell disease . Scientists comment on final draft guidance fro ...
A research team at Umeå University has created advanced light-controlled tools that allow for precise regulation of proteins ...
Panning for CTAP. By sifting through the genome of K562 myeloid progenitor cancer cells, Muhar and colleagues identified genes that mediate the breakdown of proteins (green) carrying C-terminal amides ...
CAR T cell therapy is one of the most promising new cancer treatments to emerge in recent years. It involves removing a ...
The gene therapy Casgevy, which will now be offered to some patients in England, could help people live disease-free, experts ...
Design Therapeutics' GeneTAC platform is revolutionizing genetic disease treatment with small molecules and promising results ...
CAR T cell therapy is one of the most promising new cancer treatments to emerge in recent years. It involves removing a ...